Overview


According to FutureWise analysis the market for Gaucher Disease Treatment in 2023 is US$ 2.1 billion, and is expected to reach US$ 2.51 billion by 2031 at a CAGR of 2.2%.

Gaucher disease (GD) is a metabolic disorder that affects the recycling of cellular glycolipids. It is caused by a lack of the lysosomal enzyme glucocerebrosidase EC3.2.1.45 (also known as glucosyl ceramidase or acid beta-glucosidase [GBA]). In patients with GD, glucosylceramide (also known as glucocerebroside) and several related compounds normally degraded to glucose and lipid components by glucocerebrosidase accumulate within cell lysosomes. Treatment of GD is tailored to the individual patient because of the variability in the manifestations, severity, progression of the disease, and treatment response.GD was the first inherited metabolic disorder to be treated with enzyme replacement therapy (ERT). Additional treatments include substrate reduction therapy (SRT) and supportive care measures to manage associated conditions.

Individuals with Gaucher disease experience different symptoms. Some patients of Gaucher disease exhibit just minor symptoms or none at all. Symptoms in other people can result in critical health issues and even death. Type 2 and 3 of Gaucher's illness also result in neurological (brain) issues in addition to symptoms affecting the blood, organs, and bones. These signs appear within the first six months of life in newborns with Gaucher disease type 2. At birth, they could have abnormalities in their skin. Gaucher disease type 3 symptoms start to show at the age of 10, and they get worse over time. Type 1 Gaucher disease is curable with consistent therapy. For instance, Type 1 treatments either raise enzyme levels or lower the fatty substance that builds up in the body as a result of Gaucher disease. However, the neurological damage caused by types 2 and 3 of Gaucher disease is incurable.

Lysosomal disease's increasing prevalence is anticipated to be a key factor, accelerating the market's growth pace. When an enzyme is deficient, lysosomal storage diseases, which are inherited metabolic illnesses, result in an abnormal build-up of several dangerous substances in the body's cells. Patients with Gaucher disease type I have shown to benefit from enzyme replacement therapy (ERT). Significant improvements have been made in skeletal anomalies, liver and spleen enlargement, and anaemia with low platelet counts. When receiving ERT, people with Gaucher disease types II and III also experience improvements in these systemic symptoms. In the next years, the market is anticipated to expand due to the aforementioned causes. Gaucher disease physical symptoms and indications vary widely from patient to patient. Some individuals have few or no symptoms, while others may experience severe repercussions that limit the expansion of the gaucher disease treatment market's income. In addition, less effective treatment choices like substrate reduction therapy and enzyme replacement therapy have a detrimental effect on the treatment market. Market expansion is anticipated to be hampered by the high cost of the therapy, a lack of public awareness, and poor reimbursement policies. Additionally, more R&D activities are being conducted and investment in advanced technologies are increased which are providing opportunities for key players existing in the market.

FutureWise Market Research has published a report that provides an insightful analysis of Gaucher Disease Treatment Market trends that are affecting the overall market growth. This report will provide a detailed analysis of market share, regional insights, and competitor analysis that includes stature of key manufacturers operational in this industry. According to the analysis conducted by FutureWise research analysts, the Gaucher Disease Treatment Market is estimated to register a considerable growth rate over the forecast period. This report lists the market segments and potential prospects available across this industry, in addition providing crucial information on the total valuation currently held by the industry. Moreover, this report will assist key management individuals in an organisation to enhance their decisions pertaining to business expansion as well as strategic changes for increasing customer base.

  • Abbott
  • Aptalis Pharma
  • Genzyme Corporation
  • GlaxoSmithKline (GSK)
  • Pfizer Inc.
  • Shire Human Genetic Therapies, Inc.
  • Eli Lilly and Company
  • Enobia Pharma Inc.
  • Anthera Pharmaceuticals, Inc.
  • BioMarin Pharmaceutical Inc.
  • MedPro Rx
  • Zymenex A/S
  • Merck Serono

By Disease Type

  • Type 1 (Neuropathic Forms)
  • Type 2 (Perinatal Lethal Form)
  • Type 3 (Slow-Neurologic Decay Form)

By Medication  

  • Enzyme replacement therapy (ERT)
    • Imiglucerase (Cerezyme)
    • Velaglucerase alfa (VPRIV)
    • Taliglucerase alfa (Elelyso)
    • Others
  • Substrate reduction therapy (SRT)
    • Glucosylceramide synthase inhibitors
      • Miglustat
      • Eliglustat
  • Surgical
    • Bone marrow transplant
    • Spleen Removal

By End User

  • Hospitals  
  • Ambulatory Surgical Centers
  • Clinical research institutes

By Region

  • North America
  • Europe
  • Asia-Pacific
  • Latin America
  • Middle East and Africa

This market research report also emphasis on factors affecting the growth rate in various regions listed above. A deep-down analysis of region will also be provided in the final version of this market which is based on conclusion of primary interviews and secondary data point gathered during the process.

By region, the market is segmented into North America, Latin America, Europe, Asia-Pacific, and Middle East & Africa. North America registered highest share in the market in 2022. Additionally, based on disease type; type 1, type 2, and type 3 hold 71.3%, 19.2%, and 9.4% respectively in 2022 globally. Due to the rising prevalence of the ailment and growing knowledge of the use of efficient treatment options, North America is anticipated to hold the largest market share in the market for Gaucher disease treatments. The region's market is also being driven forward by the presence of major market players there and their revenue-generating strategies.


  • Tier 1 players- established companies in the market with major market share
  • Tier 2 players
  • New Entrants
  • Emerging players which are growing rapidly
  • Growth prospects
  • SWOT analysis
  • Key trends
  • Key data points affecting market growth
  • To provide with an exhaustive analysis on the Gaucher Diseases Treatment Market By Disease Type, By Medication, By End User, By Region.
  • To cater comprehensive insights on factors such as drivers, restraints, trends, opportunity, and additionally segmental and regional factors impacting market growth.
  • To evaluate current market trends and forecast micro-markets and the overall market projections which are represented in the format of data-sets and ppt.
  • To predict the market size, in key regions— North America, Europe, Asia Pacific, Latin America and Middle East and Africa.
  • To provide information on competitors which includes landscape mapping, technological advancements, R&D spending, news concerning strategic alliances, and new product launches.
  • We have a flexible delivery model and you can suggest changes in the scope/table of content as per your requirement
  • The customization Mobility Care offered are free of charge with purchase of any license of the report
  • You can directly share your requirements/changes to the current table of content to: sales@futurewiseresearch.com

Table of Contents


  • 1.   Market Introduction
    •   1. Objectives of the Study
        2. Market Definition
        3. Market Scope
         3.1. Years Considered for the Study
         3.2. Market Covered
        4. Currency
        5. Limitations
        6. Stakeholders
  • 2.   Research Methodology
    •   1. Research Data
         1.1. Secondary Data
          1.1.1. Key Data from Secondary Sources
         1.2. Primary Data
          1.2.1. Key Data from Primary Sources
        2. Market Size Estimation
        3. Market Breakdown and Data Triangulation
        4. Assumptions for the Study
  • 3.   Executive Summary
    •   1. Market Outlook
        2. Segment Outlook
        3. Competitive Insights
  • 4.   Gaucher Disease Treatment Market Variables, Trends and Scope
    •   1. Market Lineage Outlook
        2. Penetration and Growth Prospect Mapping
        3. Industry Value Chain Analysis
        4. Cost Analysis Breakdown
        5. Technology Overview
        6. Regulatory Framework
         6.1. Reimbursement Framework
         6.2. Standards and Compliances

  • 5.   Market Overview
    •   1. Market Dynamics
         1.1. Market Driver Analysis
          1.1.1. Increasing focus of Gaucher Disease Treatment Market Companies on Brand Protection
          1.1.2. Untapped Opportunities in Emerging Regions
         1.2. Market Restraint Analysis
          1.2.1. High Cost Associated with Implementation of Predictive Analysis
         1.3. Industry Challenges
          1.3.1. Presence of Ambiguous Regulatory Framework
  • 6.   Gaucher Disease Treatment Market Analysis Tools
    •   1. Industry Analysis - Porter’s
         1.1. Supplier Power
         1.2. Buyer Power
         1.3. Substitution Threat
         1.4. Threat from New Entrants
         1.5. Competitive Rivalry
        2. Pestel Analysis
         2.1. Political Landscape
         2.2. Environmental Landscape
         2.3. Social Landscape
         2.4. Technology Landscape
         2.5. Legal Landscape
        3. Major Deals And Strategic Alliances Analysis
         3.1. Joint Ventures
         3.2. Mergers and Acquisitions
         3.3. Licensing and Partnership
         3.4. Technology Collaborations
         3.5. Strategic Divestments
        4. Market Entry Strategies
        5. Case Studies
  • 7.   Gaucher Disease Treatment Market, By Disease Type Historical Analysis and Forecast 2023-2031 (USD Million)
    •   1. Type 1 (Neuropathic Forms)
        2. Type 2 (Perinatal Lethal Form)
        3. Type 3 (Slow-Neurologic Decay Form)

  • 8.   Gaucher Disease Treatment Market, By Medication Historical Analysis and Forecast 2023-2031 (USD Million)
    •   1. Enzyme replacement therapy (ERT)
         1.1. Imiglucerase (Cerezyme)
         1.2. Velaglucerase alfa (VPRIV)
         1.3. Taliglucerase alfa (Elelyso)
         1.4. Others
        2. Substrate reduction therapy (SRT)
         2.1. Glucosylceramide synthase inhibitors
          2.1.1. Miglustat
          2.1.2. Eliglustat
        3. Surgical
         3.1. Bone marrow transplant
         3.2. Spleen Removal

  • 9.   Gaucher Disease Treatment Market, By End User Historical Analysis and Forecast 2023-2031 (USD Million)
    •   1. Hospitals
        2. Ambulatory Surgical Centers
        3. Clinical research institutes

  • 10.   North America Gaucher Disease Treatment Market Analysis 2017-2022 and Forecast 2023-2031 (USD Million)
    •   1. Introduction
        2. Historical Market Size (USD Million) Analysis By Country, 2017-2022
         2.1. U.S.A
         2.2. Canada
         2.3. Mexico
        3. Market Size (USD Million) Forecast for North America 2023-2031

  • 11.   Latin America Gaucher Disease Treatment Market Analysis 2017-2022 and Forecast 2023-2031 (USD Million)
    •   1. Introduction
        2. Historical Market Size (USD Million) Analysis By Country, 2017-2022
         2.1. Brazil
         2.2. Venezuela
         2.3. Argentina
         2.4. Rest of Latin America
        3. Market Size (USD Million) Forecast for Latin America 2023-2031

  • 12.   Europe Gaucher Disease Treatment Market Analysis 2017-2022 and Forecast 2023-2031 (USD Million)
    •   1. Introduction
        2. Historical Market Size (USD Million) Analysis By Country, 2017-2022
         2.1. Germany
         2.2. U.K
         2.3. France
         2.4. Italy
         2.5. Spain
         2.6. Russia
         2.7. Poland
         2.8. Rest of Europe
        3. Market Size (USD Million) Forecast for Europe 2023-2031

  • 13.   Asia Pacific Gaucher Disease Treatment Market Analysis 2017-2022 and Forecast 2023-2031 (USD Million)
    •   1. Introduction
        2. Historical Market Size (USD Million) Analysis By Country, 2017-2022
         2.1. Japan
         2.2. China
         2.3. India
         2.4. Australia and New Zealand
         2.5. ASEAN
         2.6. Rest of Asia Pacific
        3. Market Size (USD Million) Forecast for Asia Pacific 2023-2031

  • 14.   Middle East and Africa Market Analysis 2017-2022 and Forecast 2023-2031 (USD Million)
    •   1. Introduction
        2. Historical Market Size (USD Million) Analysis By Country, 2017-2022
         2.1. GCC
         2.2. Israel
         2.3. South Africa
         2.4. Rest of MEA
        3. Market Size (USD Million) Forecast for MEA 2023-2031

  • 15.   Market Share Analysis and Competitive Landscape
    •   1. Global Landscape - Key Players, Revenue and Presence
        2. Global Share Analysis - Key Players (Tier 1, Tier 2, Tier 3)
        3. Global Emerging Companies
        4. North America - Market Share Analysis and Key Regional Players
        5. Europe - Market Share Analysis and Key Regional Players
        6. Asia Pacific - Market Share Analysis and Key Regional Players
        7. Global Key Player - Growth Matrix
  • 16.   Company Profiles (Competition Dashboard, Competitors Deep Dive, Products Offered and Financial Layouts)
    •   1. Abbott
         1.1. Company Overview
         1.2. Product Portfolio
         1.3. SWOT Analysis
         1.4. Financial Overview
         1.5. Strategic Overview
        2. Aptalis Pharma
         2.1. Company Overview
         2.2. Product Portfolio
         2.3. SWOT Analysis
         2.4. Financial Overview
         2.5. Strategic Overview
        3. Genzyme Corporation
         3.1. Company Overview
         3.2. Product Portfolio
         3.3. SWOT Analysis
         3.4. Financial Overview
         3.5. Strategic Overview
        4. GlaxoSmithKline (GSK)
         4.1. Company Overview
         4.2. Product Portfolio
         4.3. SWOT Analysis
         4.4. Financial Overview
         4.5. Strategic Overview
        5. Pfizer Inc.
         5.1. Company Overview
         5.2. Product Portfolio
         5.3. SWOT Analysis
         5.4. Financial Overview
         5.5. Strategic Overview
        6. Shire Human Genetic Therapies, Inc.
         6.1. Company Overview
         6.2. Product Portfolio
         6.3. SWOT Analysis
         6.4. Financial Overview
         6.5. Strategic Overview
        7. Eli Lilly and Company
         7.1. Company Overview
         7.2. Product Portfolio
         7.3. SWOT Analysis
         7.4. Financial Overview
         7.5. Strategic Overview
        8. Enobia Pharma Inc.
         8.1. Company Overview
         8.2. Product Portfolio
         8.3. SWOT Analysis
         8.4. Financial Overview
         8.5. Strategic Overview
        9. Anthera Pharmaceuticals, Inc.
         9.1. Company Overview
         9.2. Product Portfolio
         9.3. SWOT Analysis
         9.4. Financial Overview
         9.5. Strategic Overview
        10.BioMarin Pharmaceutical Inc.
         10.1. Company Overview
         10.2. Product Portfolio
         10.3. SWOT Analysis
         10.4. Financial Overview
         10.5. Strategic Overview
        11. MedPro Rx
         11.1. Company Overview
         11.2. Product Portfolio
         11.3. SWOT Analysis
         11.4. Financial Overview
         11.5. Strategic Overview
        12. Zymenex A/S
         12.1. Company Overview
         12.2. Product Portfolio
         12.3. SWOT Analysis
         12.4. Financial Overview
         12.5. Strategic Overview
        13. Merck Serono
         13.1. Company Overview
         13.2. Product Portfolio
         13.3. SWOT Analysis
         13.4. Financial Overview
         13.5. Strategic Overview

  • 17.   Pre and Post COVID-19 Impact
    •   1. Positive influence on the healthcare industry
        2. The financial disruption of the manufacturing sector
        3. Impact of COVID-19 on emerging companies
        4. Significant mandates in the regulations initiated by healthcare administrations
        5. The overall economic slowdown of the developing and developed nations
  • 18.   FutureWise SME Key Takeaway Points for Client

FAQ


The report provides in-depth analysis of the latest trends, including advancements in gene therapy, new drug developments, and shifts in patient care strategies. It is frequently updated to reflect emerging developments and changes in the market landscape.

The latest advancements in Gaucher treatment include new enzyme replacement therapies and substrate reduction therapies that aim to reduce or manage symptoms more effectively. Additionally, gene therapy trials are underway with the potential to provide long-term solutions for those affected by the disease.

The market size for Gaucher Disease treatment helps propel research and development for new medications. A larger market size often means more investment into finding better and more efficient treatments, which can lead to increased availability and improved access to medications for patients.

Yes, research in Gaucher disease is continuous, with efforts focused on gene therapy, new pharmaceuticals, and improved therapeutic approaches. These advancements aim to provide more effective and less burdensome treatments for those affected.

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