Spinal Muscular Atrophy Treatment Market is poised to register a CAGR of 28.9% during the forecast period 2022 to 2028. 

Rising awareness pertaining to spinal muscular atrophy, soaring initiatives from improving treatment alternatives for rare diseases are some of the crucial factors contributing to the growth of the market. For instance, the U.S FDA awarded an orphan drug license to the collaborative program of SMA Foundation, PTC Therapeutics and Roche named RG7916 for treating spinal muscular atrophy. Furthermore, the growing initiatives implemented by different non-profit and public organizations for creating awareness pertaining to SMA has boosted the spinal muscular atrophy treatment market growth. Additionally, the National Institute for Care and Health Excellence in January 2018, summoned Biogen for submitting a tech appraisal for Spinraza. NHs and NICE have agreed for a long-term plan regarding Biogen’s Spinraza. Such a wide range of products for treating SMA has propelled the proliferation of the market. 

Market Segmentation:

By Treatment
•    Drugs
•    Gene Therapy

By Route of Administration
•    Oral
•    Intrathecal

By Disease Type 
•    Type 1
•    Type 2
•    Type 3
•    Type 4

By Region
•    North America
•    Europe
•    Asia-Pacific
•    Latin America
•    Middle East and Africa

The market is classified into treatment, route of administration, disease type and region. The treatment segment is fragmented into gene therapy and drugs. The gene therapy segment is anticipated to hold the largest spinal muscular atrophy treatment market share as it is a viable option than drugs. Additionally, Spinraza is the only drug that received an FDA approval for SMA treatment in recent times which is why it is expected that the drugs segment is predicted to grow at a substantial rate during the forecast period. The route of administration segment is classified into oral and intrathecal. The intrathecal segment is anticipated to lead the market as drugs like Spinraza are provided intrathecally. Additionally, no new drugs are expected to be launched till the end of 2021 which shall maintain its market dominance.
The disease type segment is categorised into type 1, type 2, type 3 and type 4. The type 1 segment is estimated to lead the market owing to its rising prevalence. Furthermore, companies are emphasizing on developing drugs for treating type 1 SMA and this shall boost the segment growth. Similarly, there have been significant progress in the development of novel therapies. For instance, AveXis Inc. have developed a gene therapy, AVXS-101, which has been tested clinically for safety evaluations. Similarly, Novartis AG’s LMI07 also focusses on treating type 1 SMA. 

Regional Analysis:

The North America region is predicted to dominate the market as the Unites States market generates maximum revenue amongst all regions. Furthermore, crucial players like Biogen are in the region as they have developed important drugs like Spinraza. Moreover, there has been a rise in the number of initiatives conducted by private and public bodies for creating awareness coupled with growing investments in research and development activities related to spinal muscular atrophy.

Competitive Landscape:                            

Some of the major players of the market are Biogen, Ionis Pharmaceuticals Inc., F. Hoffmann La Roche Ltd., Avenis Inc., Novartis AG, Cytokinetics Inc.

FutureWise Key Takeaways:

•    Growth prospects
•    SWOT analysis 
•    Key market trends 
•    Key data-points affecting market growth

Objectives of the Study:

•    To provide with an exhaustive analysis on the global spinal muscular atrophy treatment market by treatment, by route of administration, by disease type and by region
•    To cater comprehensive information on factors impacting market growth (drivers, restraints, opportunities, and industry-specific restraints)
•    To evaluate and forecast micro-markets and the overall market 
•    To predict the market size, in key regions (along with countries)— North America, Europe, Asia Pacific, Latin America and Middle East and Africa
•    To record, evaluate and analyze competitive landscape mapping- product launches, technological advancements, mergers and expansions

Flexible Delivery Model:

•    We have a flexible delivery model and you can suggest changes in the scope/table of content as per your requirement
•    The customization Mobility Care offered are free of charge with purchase of any license of the report
•    You can directly share your requirements/changes to the current table of content to: sales@futurewiseresearch.com


Need Assistance


UK : +44 141 628 9353
US : +1 347 709 4931


Contact Sales

What you get

  • Excel Dataset

  • Infographics

  • PDF Report

  • Market Overview

  • PowerPoint Presentation

What's included

  • Consumer Perception and Procurement

  • Competitive Analysis

  • What’s Next

  • Market Data Forecast

  • Risks and Opportunity Assessment

  • Market Trends and Dynamics